At Research SMA, 2024 was a year of progress, passion, and real impact. We are proud to share the highlights of our Annual Report 2025 — a testament to what can be achieved when a community comes together with a shared mission: to support families affected by Spinal Muscular Atrophy (SMA) and accelerate clinical research that changes lives.
Our charitable purpose remains firmly rooted in two key pillars:
Thanks to your support, we turned these aims into measurable action throughout 2024.
A highlight of our year was the incredible 100 WALK 100 event. In June 2024, over 100 participants walked 100 miles along the Cotswold Way over three days.
Your generosity enabled us to fund two major research projects in 2024:
Pledged to Great Ormond Street Hospital and ICANS, Milan, Italy, to launch the two-year nutritional study ‘SMA4Nutrition’. Early results are expected in 2026/27.
Awarded to the University of Oxford to fund the clinical trial ‘ACESMA’, exploring physiotherapy for children with SMA.
These initiatives represent hope, innovation, and the power of partnership, far beyond the numbers.
Building on a successful year, we’re excited to be in discussions with NHS Sheffield Children’s Hospital about a new clinical research project: ‘SMA Spinal Management Study’. We’ll keep supporters updated as plans develop throughout 2025.
We extend our heartfelt thanks to everyone who supported us in 2024. Whether you donated, walked, volunteered, or shared our story, you are part of the change.
As a charity led by a passionate group of trustees and powered by community spirit, we couldn’t do this without you.
Here’s a snapshot of our financial activity in 2024:
£132,187 raised through fundraising
£165,396 directed to charitable activities
£143,492in reserves as of January 2025, including £41,604 committed to ongoing projects
